The USA has approved the Casgevy drug, which uses the CRISPR gene editing system. This is stated in Message On the US Food and Drug Administration (FDA) website.
It was noted that the drug will be used to treat sickle cell anemia, a hereditary pathology of the abnormal structure of the blood protein hemoglobin. About 100 thousand people in the United States suffer from this pathology.
“Gene therapy promises to provide more targeted and effective treatments, especially for people with rare diseases for which current treatment options are limited,” the release states.
Before this portal SciTechDaily reportedHe said that scientists from the University of Basel have discovered a new treatment method that may be effective in restoring hearing. Researchers suggest that interfering with the signaling pathways that control the function of auditory sensory cells could restore natural hearing ability.
Previously in Russian pharmacies stated about the lack of a popular antidepressant.